Peripheral Programs
DISCOVERY
PRECLINICAL
CLINICAL
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CTX001 Iron Mobilizer
Small molecule
CKD Anemia
H2 2026: P1 HV Data
Undisclosed
CTX201
siRNA
Inflammatory Anemia
CTX211
siRNA
Myelofibrosis Anemia
Discovery
siRNA/ASO
Hematologic Disorders
CNS Programs
Iron Mobilizer
Small molecule
Parkinson’s Disease