pipeline
Cajal’s Focus on Restoring Iron Homeostasis
Peripheral Programs
DISCOVERY
PRECLINICAL
CLINICAL
next milestone
CTX001 Iron Mobilizer
Small molecule
CKD Anemia
H1 2026: Phase 1 Start
Undisclosed
CTX201
siRNA
Inflammatory Anemia
Discovery
siRNA/ASO
Hematologic Disorders
CNS Programs
Iron Mobilizer
Small molecule
Parkinson’s Disease
Friedreich’s Ataxia
Undisclosed
Small molecule
CNS Diseases
Undisclosed
siRNA/ASO
Parkinson’s Disease
