pipeline

Cajal’s Focus on Restoring Iron Homeostasis

Peripheral Programs

DISCOVERY

PRECLINICAL

CLINICAL

next milestone

CTX001 Iron Mobilizer

Small molecule

CKD Anemia

H2 2026: P1 HV Data

Undisclosed

CTX201

siRNA

Inflammatory Anemia

CTX211

siRNA

Myelofibrosis Anemia

Discovery

siRNA/ASO

Hematologic Disorders

CNS Programs

Iron Mobilizer

Small molecule

Parkinson’s Disease

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